PTC 124 is for Duchenne muscular dystrophy and not for congenital muscular dystrophy...on other proteins. Read more: http://www.emedicine.com/neuro/topic549.htm PTC 124 is used to halt the process causing Duchenne muscular...
1 Answers · Science & Mathematics · 30/04/2007
...candidate from a New Jersey-based company (PTC124 from PTC Therapeutics ) is in Phase II clinical trials for DMD as well...
2 Answers · Science & Mathematics · 06/02/2011